Following Parent Project Muscular Dystrophy's news feed is very easy. Subscribe using the "follow" button on the top right and if you want to, choose the updates by topic or tag.
We will deliver them to your inbox, your phone, or you can use follow.it like your own online RSS reader. You can unsubscribe whenever you want with one click.
Keep up to date with Parent Project Muscular Dystrophy!
Parent Project Muscular Dystrophy: Parent Project Muscular Dystrophy (PPMD) | Fighting to End Duchenne
Is this your feed? Claim it!
PPMD has a long history of working alongside our community to document treatment preferences and share those insights with regulatory authorities such as the FDA. Through town halls, listening sessions, and conversations at community events, we consistently hear that stability is a critically important (transformative) outcome in both care and treatment. There is no consensus...
Sarepta Therapeutics, Inc. has shared that the U.S. Food and Drug Administration (FDA) has approved dosing in Cohort 8 of ENDEAVOR, an open-label, Phase 1b study assessing the expression and safety of ELEVIDYS in multiple cohorts of individ...
Recently, the Duchenne and Becker community gathered virtually for the final PPMD Together meeting of the year. This intimate session centered on fostering friendships for everyone in the family while living with dystrophinopathy.
The meeting, led by PPMD’s CEO, Katherine Beaverson, emp...
Avidity Biosciences, Inc. has announced its Managed Access Program (MAP) for delpacibart zotadirsen (del-zota) for eligible individual...
The second session in PPMD’s Becker Muscular Dystrophy webinar series focused on cardiopulmonary care. Our clinical experts reviewed what every person living with Becker and their families should know about care for the heart and lungs.
Speakers:
